Real-to-Reel Movie Raises Awareness of Pompe Disease

Summary

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In preparation for his role as Dr. Preston in the movie "Extraordinary Measures," actor P.J. Byrne paid a visit to Dr. Perry Shieh, a clinical neurophysiologist at the Ronald Reagan UCLA Medical Center.

Byrne was there to learn from a real doctor what it's like to tell parents there is no cure for their child's medical condition.

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Extract

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Real-to-Reel Movie Raises Awareness of Pompe Disease

"Extraordinary Measures" gives a dramatic account of the science and determination that led to the development of a drug to treat Pompe.

Though the story may be part fact, part fiction, the treatment is real.

In 2006, the Food and Drug Administration gave its approval to Genzyme Corp. to market the drug Myozyme in the United States...

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